Metagenomi says it hopes to start clinical trials next year to test MGX-001, its gene-editing therapy candidate for ...
Be Biopharma has raised $92 million to support the first-in-human Phase 1/2 trial of BE-101, which is made to lower bleeding ...
Columnist Alliah Czarielle shares how video games helped her husband cope with hemophilia bleeds in the hospital when he was a child.
Two hemophilia patients in the U.S. who struggled for years with bleeds have been given Hemgenix, the first gene therapy ...
Now that his adult sons are managing their own hemophilia care, columnist Joe MacDonald is able to consider moving for a job.
Columnist Jennifer Lynne interviews Debbie Murray, a New Yorker whose hemophilia B diagnosis didn't occur until she was almost 51.
Topping the list at No. 1 was my column paying tribute to Michaela DePrince and her mother, Elaine. Michaela, a world-renowned ballerina, died Sept. 10 at age 29, just a day before her adoptive mother ...
MacDonald worries about her adult son being complacent when it comes to administering his hemophilia medication.